RP-L102, which the firm designed to treat a form of disease caused by FANCA mutations, is already under review with the European Medicines Agency.

Rocket Pharmaceuticals is also progressing in its other projects, like the rolling BLA for Fanconi anemia and the Phase 1 enrollment completion in PKP2-arrhythmogenic cardiomyopathy. Furthermore, the ...

Fanconi anemia has no known cure and can cause bone marrow failure and cancer. So Jimbo and his ex-wife, Candi Fisher, established the Kidz 1st Fund in 2011 to help spread awareness and raise ...

In case, your uric acid levels are low, you can get Wilson's disease, a condition that leads to a build-up of copper in the body or Fanconi syndrome, a kidney tube disorder. There are various tests to ...

According to the Japanese Society of Nephrology, many people who fell ill after ingesting Kobayashi Pharmaceutical’s benikoji supplements are suspected of having developed Fanconi syndrome ...

The genetic basis of Fanconi anemia (FA) is mysterious and complex, as none of the five genes previously associated with the disorder have homology to genes encoding proteins of known function.

Live webcasts of the presentations will be available on the Events & News – Events page of Jasper's Investor Relations website. An archived replay of each presentation will be available on Jasper's ...

In most cases, glycosuria develops because of high blood sugar or diabetes, symptoms may include: While less common, Fanconi syndrome (a condition that affects the kidneys) can also cause glycosuria.

He has raised more than £8,000 for a group of charities, including Fanconi Hope, which supports children affected by fanconi anemia, a rare genetic disorder affecting bone marrow. "It was really ...

RCKT incurs narrower-than-expected third-quarter 2024 loss. The company provides updates on its pipeline candidates.

Its clinical program is an LVV-based gene therapy for the treatment of Fanconi Anemia (FA), a difficult to treat genetic disease that leads to bone marrow failure and potentially cancer.