The startup’s technology combines an AAV — a common gene therapy delivery tool — with an immunotherapy approach now widely used in oncology. The idea is to give patients a one-time treatment that ...

Headlines,CRISPR Therapeutics,(NASDAQ:CRSP),has achieved a significant regulatory milestone with its gene-editing therapy, Casgevy, now approved in multiple countries, but has faced challenges in ...

A new start­up at­tempt­ing to de­vel­op AAV gene ther­a­pies to treat can­cer emerged from stealth Thurs­day morn­ing with $26 mil­lion in seed fund­ing — and a … ...

Vironexis Biotherapeutics has unveiled with $26 million and a clinical-trial-ready gene therapy that has already nabbed FDA fast track and rare pediatric disease tags. The San Diego-based biotech ...

"The era of gene therapy for neuromuscular diseases has begun, and the complexity of these diseases requires us to constantly innovate to improve drug candidates targeting muscle. The new ...

Soo-Kyung Lee hoped to change that through gene therapy. However, some had doubts that because of FOXG1’s role in brain development in utero, administering a therapy after birth may not have a ...

SINGAPORE – Patients here who require certain costly cell, tissue and gene therapy products (CTGTPs) will now be eligible for subsidies, starting with one product for blood cancers. This opens ...

It's gene therapy research at Children's Hospital of Philadelphia that's being called a game changer. The first patient to get the therapy outside a research setting is a Cherry Hill college ...

BridgeBio Pharma is slashing its gene therapy budget and pulling back from the modality after seeing the results of a phase 1/2 clinical trial. CEO Neil Kumar, Ph.D., said the data “are not yet ...

The Asia-Pacific gene therapy market was valued at $349.1 million in 2020 and is expected to grow at a compound annual growth rate (CAGR) of 36.8% to reach nearly $7 billion in 2030. This ...

Sow and Friedman are serious about friendship—they co-wrote the book Big Friendship: How We Keep Each Other Close—so they tried something a bit unconventional: friendship therapy. Just like in ...

A new study from the University of Copenhagen reveals that a specific gene plays a significant role in determining longevity, potentially opening the door to new treatments. Sleep, fasting, exercise, ...