It acquired rights to taligurase alfa, a form of the enzyme glucocerebrosidase in development for the treatment of Gaucher's disease, from Protalix Biotherapeutics in Carmiel, Israel. Protalix has ...
As per the National Gaucher Foundation, this disease was first discovered by a French doctor, Philippe Gaucher, after whom it ...
VQ-101 is an oral, small molecule allosteric activator targeting the lysosomal enzyme glucocerebrosidase (GCase) that is undergoing evaluation as a potential treatment for Parkinson’s disease in ...